As gene therapies falter on the market, this biopharma is aiming to defy the odds

After a strong launch for its cancer gene therapy, Ferring Pharmaceuticals is setting the stage for long-term growth.

By Meagan Parrish • Aug. 8, 2025

Inside AstraZeneca’s long-game strategy in lung cancer

New long-term results for Tagrisso in EGFR-mutated non-small cell lung cancer showcase a precision approach the company has honed for decades.

By Michael Gibney • Aug. 7, 2025

Explore the Trendline➔

Rare diseases

As drug developers find promise in the rare diseases, deals and treatments are on the rise

By PharmaVoice staff

PBM reform was dropped from Trump’s spending bill. It could have saved billions.

The Senate nixed a provision to “delink” drug list prices from compensation for PBMs and other drug middlemen days before its passage.

By Alexandra Pecci • Aug. 6, 2025

David Altshuler, geneticist who helped transform Vertex, to retire next year

Since becoming Vertex's top scientist in 2015, Altshuler has helped the company become an industry powerhouse. He’ll depart next year in a “planned transition.”

By Ben Fidler • Aug. 5, 2025

Let’s make a deal? Big Pharma execs express varying views on their M&A future

Pharma executives are keeping their eyes open for dealmaking opportunities as every company has its own battles to fight.

By Michael Gibney • Aug. 5, 2025

Drugmakers score policy win in a prolonged fight against 340B

A new pilot program from HHS would alter the contentious 340B pricing program by swapping traditional upfront drug discounts for rebates.

By Amy Baxter • Aug. 4, 2025

Merck & Co. assembles an Alzheimer’s comeback with a next-gen precision focus

With two molecules in mid-stage trials, the pharma giant is taking another swing at the difficult disease with a greater understanding of its drivers.

By Michael Gibney • Aug. 1, 2025

C-suite shuffles ripple through pharma

Novo Nordisk, Kenvue and Jazz Pharmaceuticals announced changes at the top this month.

By Meagan Parrish • July 31, 2025

Dr. Vinay Prasad, controversial FDA official, abruptly departs agency

Prasad's exit ends a tumultuous tenure during which he led a reworking of agency guidelines on COVID vaccines and his office got embroiled in controversy over a Duchenne gene therapy.

By Ben Fidler • July 30, 2025

Roche pushes ahead with late-comer strategy in obesity

The Swiss pharma company announced several updates to its obesity portfolio in its latest earnings report.

By Amy Baxter • July 30, 2025

Could bispecifics unseat Keytruda from its oncology throne?

Signals suggest the drugs could improve on the standard of care, but the market may not make it easy for another megablockbuster to rise to the top.

By Kelly Bilodeau • July 28, 2025

From the bench: Researchers make NIH-funded preclinical strides in mRNA and obesity

The studies are contributing preclinical advances for some of the world’s biggest blockbusters.

By Michael Gibney • July 25, 2025

Pharma’s turbo spending spree on US manufacturing

The industry’s push to expand American drug production isn’t abating as threats of tariffs loom.

By Meagan Parrish • July 24, 2025

How Bristol Myers Squibb uses AI to validate drugs before they’re even in the lab

The company’s AI approach allows molecule candidates to be vetted for efficacy and other properties early in development.

By Alexandra Pecci • July 24, 2025

Who is Dr. George Tidmarsh, the new director of CDER?

Despite past criticism of public health policies, Tidmarsh recently praised the FDA and said he’ll focus on boosting review efficiencies.

By Meagan Parrish and Michael Gibney • July 23, 2025

Novartis’ Zolgensma sales fall again as gene therapy market woes persist

Novartis has seen sales decline in a difficult gene therapy market. Is there hope on the horizon?

By Michael Gibney • July 22, 2025

3 major patent losses this year — and a key strategy to fill the gaps

Despite promising pipelines, most new launches are missing sales targets, forcing pharmas to rethink sales strategies.

By Kelly Bilodeau • July 21, 2025

Why FDA’s CRL release could open the door to lawsuits against pharma

In a push for “radical transparency” the FDA released 200 CRLs for drugs that were later approved — some of which are now public for the first time.

By Meagan Parrish • July 18, 2025

J&J accelerates past Stelara’s fall with better-than-expected portfolio growth

Stelara is faltering due to biosimilar entries, but J&J execs demonstrate they were ready to fill the gap all along.

By Michael Gibney • July 17, 2025

FDA invites more data from abroad — with a wary eye on China

The FDA approved four drugs last year without any U.S. trial participants, but has maintained a tougher stance on China, even as it grows into an R&D powerhouse.

By Amy Baxter • July 16, 2025

Need a DTC platform? Here’s how one company built its own.

Currax Pharmaceuticals was ahead of the curve when it set up a direct access platform for its obesity med. 

By Amy Baxter • July 14, 2025

With Verona deal, Merck wagers on strength of lung drug’s patents

The main patent for Ohtuvayre, the COPD drug at the heart of Verona’s $10 billion sale, expired in 2020. For Merck to make good on the deal, other secondary patents will need to hold up.

By Jonathan Gardner • July 11, 2025

Pricing watchdog will take on the rising cost of drugs at launch

ICER’s upcoming report could shed light on how the launch price of newly approved drugs affects overall cost and access from a patient perspective.

By Michael Gibney • July 10, 2025

Trump says ‘very high’ pharmaceutical tariffs coming soon

While Trump indicated drug levies would be as high as 200%, he added that pharma firms would first be given time to bring manufacturing back to the U.S.

By Philip Neuffer • July 9, 2025

As its cancer vaccine moves through the clinic, Transgene sets sights on manufacturing

Simone Steiner recently joined the French company to set the stage for launch.  

By Amy Baxter • July 9, 2025